Editorial
doi: 10.1056/NEJMe0803081.
Epub 2008 Apr 27.
Preliminary results of gene therapy for retinal degeneration
- PMID: 18441372
- DOI: 10.1056/NEJMe0803081
Item in Clipboard
Editorial
Preliminary results of gene therapy for retinal degeneration
N Engl J Med.
.
No abstract available
Comment on
-
Safety and efficacy of gene transfer for Leber's congenital amaurosis.N Engl J Med. 2008 May 22;358(21):2240-8. doi: 10.1056/NEJMoa0802315. Epub 2008 Apr 27. N Engl J Med. 2008. PMID: 18441370 Free PMC article. Clinical Trial.
-
Effect of gene therapy on visual function in Leber's congenital amaurosis.N Engl J Med. 2008 May 22;358(21):2231-9. doi: 10.1056/NEJMoa0802268. Epub 2008 Apr 27. N Engl J Med. 2008. PMID: 18441371 Clinical Trial.
Similar articles
-
Effect of gene therapy on visual function in Leber's congenital amaurosis.N Engl J Med. 2008 May 22;358(21):2231-9. doi: 10.1056/NEJMoa0802268. Epub 2008 Apr 27. N Engl J Med. 2008. PMID: 18441371 Clinical Trial.
-
[First results of gene therapy for Leber congenital amaurosis].Rev Med Suisse. 2008 May 7;4(156):1177. Rev Med Suisse. 2008. PMID: 18630174 French. No abstract available.
-
Safety and efficacy of gene transfer for Leber's congenital amaurosis.N Engl J Med. 2008 May 22;358(21):2240-8. doi: 10.1056/NEJMoa0802315. Epub 2008 Apr 27. N Engl J Med. 2008. PMID: 18441370 Free PMC article. Clinical Trial.
-
An overview of Leber congenital amaurosis: a model to understand human retinal development.Surv Ophthalmol. 2004 Jul-Aug;49(4):379-98. doi: 10.1016/j.survophthal.2004.04.003. Surv Ophthalmol. 2004. PMID: 15231395 Review.
-
Prospects for retinal gene replacement therapy.Trends Genet. 2009 Apr;25(4):156-65. doi: 10.1016/j.tig.2009.02.003. Epub 2009 Mar 18. Trends Genet. 2009. PMID: 19303164 Review.
Cited by
-
Retinal pigment epithelium differentiation of stem cells: current status and challenges.Crit Rev Biomed Eng. 2009;37(4-5):355-75. doi: 10.1615/critrevbiomedeng.v37.i4-5.30. Crit Rev Biomed Eng. 2009. PMID: 20528731 Free PMC article. Review.
-
Leber congenital amaurosis due to RPE65 mutations and its treatment with gene therapy.Prog Retin Eye Res. 2010 Sep;29(5):398-427. doi: 10.1016/j.preteyeres.2010.04.002. Epub 2010 Apr 24. Prog Retin Eye Res. 2010. PMID: 20399883 Free PMC article. Review.
-
Gene therapy for leber congenital amaurosis caused by RPE65 mutations: safety and efficacy in 15 children and adults followed up to 3 years.Arch Ophthalmol. 2012 Jan;130(1):9-24. doi: 10.1001/archophthalmol.2011.298. Epub 2011 Sep 12. Arch Ophthalmol. 2012. PMID: 21911650 Free PMC article. Clinical Trial.
-
High-titre retroviral vector system for efficient gene delivery into human and mouse cells of haematopoietic and lymphocytic lineages.J Gen Virol. 2010 Aug;91(Pt 8):1909-1918. doi: 10.1099/vir.0.020255-0. Epub 2010 Apr 21. J Gen Virol. 2010. PMID: 20410313 Free PMC article.
-
Proteomic profiling of salivary gland after nonviral gene transfer mediated by conventional plasmids and minicircles.Mol Ther Methods Clin Dev. 2014;1:14007. doi: 10.1038/mtm.2014.7. Mol Ther Methods Clin Dev. 2014. PMID: 25414909 Free PMC article.
Publication types
MeSH terms
LinkOut - more resources
Full Text Sources
Medical
