Review
doi: 10.1089/hum.2005.16.1133.
Gene therapy of storage disorders by retroviral and lentiviral vectors
Affiliations
- PMID: 16218774
- DOI: 10.1089/hum.2005.16.1133
Item in Clipboard
Review
Gene therapy of storage disorders by retroviral and lentiviral vectors
Hum Gene Ther.
2005 Oct.
No abstract available
Similar articles
-
Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New Indications.Mol Ther. 2017 May 3;25(5):1155-1162. doi: 10.1016/j.ymthe.2017.03.025. Epub 2017 Apr 4. Mol Ther. 2017. PMID: 28389320 Free PMC article. Review.
-
Advances in lentiviral vector design for gene-modification of hematopoietic stem cells.Curr Opin Biotechnol. 2002 Oct;13(5):429-36. doi: 10.1016/s0958-1669(02)00346-4. Curr Opin Biotechnol. 2002. PMID: 12459333 Review.
-
Gene therapy for lysosomal storage disorders.Expert Opin Biol Ther. 2001 Sep;1(5):857-67. doi: 10.1517/14712598.1.5.857. Expert Opin Biol Ther. 2001. PMID: 11728220 Review.
-
Gene therapy for the neurological manifestations in lysosomal storage disorders.J Lipid Res. 2014 Sep;55(9):1827-38. doi: 10.1194/jlr.R047175. Epub 2014 Mar 29. J Lipid Res. 2014. PMID: 24683200 Free PMC article. Review.
-
Lentiviral hematopoietic stem cell gene therapy in inherited metabolic disorders.Hum Gene Ther. 2014 Oct;25(10):862-5. doi: 10.1089/hum.2014.102. Epub 2014 Sep 17. Hum Gene Ther. 2014. PMID: 25184354 Free PMC article. Review.
Cited by
-
Functional rescue in an Angelman syndrome model following treatment with lentivector transduced hematopoietic stem cells.Hum Mol Genet. 2021 Jun 9;30(12):1067-1083. doi: 10.1093/hmg/ddab104. Hum Mol Genet. 2021. PMID: 33856035 Free PMC article.
-
Gene therapy approaches for lysosomal storage disease: next-generation treatment.Hum Gene Ther. 2012 Aug;23(8):808-15. doi: 10.1089/hum.2012.140. Hum Gene Ther. 2012. PMID: 22794786 Free PMC article. Review.
-
Modest phenotypic improvements in ASA-deficient mice with only one UDP-galactose:ceramide-galactosyltransferase gene.Lipids Health Dis. 2006 Aug 7;5:21. doi: 10.1186/1476-511X-5-21. Lipids Health Dis. 2006. PMID: 16893448 Free PMC article.
-
Simplified production and concentration of lentiviral vectors to achieve high transduction in primary human T cells.BMC Biotechnol. 2013 Nov 12;13:98. doi: 10.1186/1472-6750-13-98. BMC Biotechnol. 2013. PMID: 24215295 Free PMC article.
-
Targeting of the CNS in MPS-IH using a nonviral transferrin-alpha-L-iduronidase fusion gene product.Mol Ther. 2008 Aug;16(8):1459-66. doi: 10.1038/mt.2008.119. Epub 2008 Jun 3. Mol Ther. 2008. PMID: 18523448 Free PMC article.
Publication types
MeSH terms
Grants and funding
LinkOut - more resources
Full Text Sources
Medical
